On February 29, orphan drugs have their day of action: Orphan drugs is the name for drugs that target so-called rare dise\u00adases. So this action day is actually only topical every four years \u2014 rare, that is. But don\u2019t worry, in non-leap years, Rare Disease Day falls on February 28.<\/p>\n
Rare is a rela\u00adtive term:<\/p>\n
- A rare disease affects no more than 5 in 10,000 people. On the medi\u00adca\u00adtion side, the numbers look like this<\/p>\n - In October 2021, 132 drugs <\/strong>were approved as orphan drugs in the EU So times seem to be impro\u00adving for orphan drugs. Accor\u00adding to esti\u00admates by Evalua\u00adte\u00adPharma, sales of orphan drugs will increase to $273 billion <\/strong>by 2026 \u2014 twice as much as in 2020.<\/p>\n","protected":false},"excerpt":{"rendered":" On February 29, orphan drugs have their day of action: Orphan drugs is the name for drugs that target so-called rare dise\u00adases. So this action day is actually only topical every four years \u2014 rare, that is. But don\u2019t worry, in non-leap years, Rare Disease Day falls on February 28. Rare is a rela\u00adtive term: \u2014 [\u2026]<\/p>\n","protected":false},"author":4,"featured_media":1306,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"","_et_pb_old_content":"","_et_gb_content_width":"","wp_typography_post_enhancements_disabled":false,"footnotes":""},"categories":[20],"tags":[],"class_list":["post-1308","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-blog-en"],"yoast_head":"\n
\n\u2014 Depen\u00adding on the source, there are more than 6,000 to 8,000 rare dise\u00adases<\/strong>.
\n\u2014 It is esti\u00admated that four million people<\/strong> are affected in Germany.
\n\u2014 There could be 30 million suffe\u00adrers<\/strong> in the Euro\u00adpean Union.<\/p>\n
\n\u2014 The most expen\u00adsive drug in the world curr\u00adently costs over 3 million euros<\/strong>: the orphan drug Hemgenix from the US manu\u00adfac\u00adturer CSL Behring was approved in the EU in February 2023 and is effec\u00adtive against severe and mode\u00adrate hemo\u00adphilia B even in a single dose.
\n\u2014 By 2026, orphan drugs are expected to account for nearly one-third of global drug deve\u00adlo\u00adp\u00adment<\/strong>, accor\u00adding to statis\u00adtics plat\u00adform Statista<\/p>\n